Ataluren, a New Therapeutic for Alpha-1 Antitrypsin-Deficient Individuals with Nonsense Mutations.
Emer P ReevesCiara A O'DwyerDanielle M DunleaMark R WormaldPadraig HawkinsMohammad AlfaresDarrell N KottonSteven M RoweAndrew A WilsonNoel G McElvaneyPublished in: American journal of respiratory and critical care medicine (2019)
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