Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy.
Laura ObiciSenda Ajroud-DrissKon-Ping LinJohn L BerkJulian D GillmoreParag KaleHaruki KoikeDavid DaneseEmre AldincChongshu ChenJohn VestDavid Adamsnull nullPublished in: Neurology and therapy (2023)
ClinicalTrials.gov: NCT03759379.
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