Biomarkers of therapeutic efficacy in adolescents and adults with 5q spinal muscular atrophy: a systematic review.
Maria GavriilakiVasileios PapaliagkasAlexandra StampernaMaria MoschouKonstantinos NotasSotirios PapagiannopoulosMarianthi ArnaoutoglouVasilios K KimiskidisPublished in: Acta neurologica Belgica (2022)
PROSPERO CRD42021245516.
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