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Compound Heterozygous Mutations in TGM1 Causing a Severe Form of Lamellar Ichthyosis: A Case Report.

Jing ZengBaihui ShanLu GuoSha LvFuqiu Li
Published in: Pharmacogenomics and personalized medicine (2022)
We aimed to detect the pathogenic gene mutations in a patient with lamellar ichthyosis (LI). The genomic DNA of the patient was examined using high-throughput whole-exome sequencing to identify the causative mutations. Compound heterozygous mutations of c.1187G>T (p.Arg396Leu) and c.607C>T (p.Gln203*) were found in the transglutaminase-1 gene ( TGM1 ) on chromosome 14 of the proband. The mutations stated above have been reported to impair the function of TGM1 protein and to be pathogenic. Our data suggest that the proband carried compound heterozygous mutations of c.1187G>T(p.Arg396Leu) and c.607C>T(p.Gln203*) in TGM1, which were in the trans position and the cause of his disease. We also found some dermoscopic in this patient which may be specific in LI.
Keyphrases
  • early onset
  • high throughput
  • case report
  • copy number
  • genome wide
  • machine learning
  • big data
  • single molecule
  • circulating tumor
  • artificial intelligence
  • amino acid