Treatment preference among patients with spinal muscular atrophy (SMA): a discrete choice experiment.
Alisha MonnetteEr ChenDongzhe HongAlessandra BazzanoStacy DixonW David ArnoldLizheng ShiPublished in: Orphanet journal of rare diseases (2021)
Improvements in motor/breathing function, broad indication, oral or one-time infusion, and minimal risk were preferred treatment attributes. Treatment decisions should be made in clinical context and be tailored to patient needs.
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