Hematopoietic stem cell transplantation in two sisters with bone marrow failure associated with POLE gene variants.
Kentaro FujimoriNorihito IkenobeYoshihiro GochoToru UchiyamaTakao DeguchiHirotoshi SakaguchiMasanori YoshidaIchiro TakeuchiHirotaka ShimizuKatsuhiro AraiAkira IshiguroKimikazu MatsumotoAkihiro IguchiPublished in: Pediatric blood & cancer (2024)