Natural history study of factor IX deficiency with focus on treatment and complications (B-Natural).
Amy D ShapiroMargaret V RagniMunira BorhanyYasmina L AbajasMichael D TarantinoKatharina HolsteinStacy E CroteauRiana LiesnerCristina TarangoManuela CarvalhoCatherine E McGuinnEva FundingChristine L KemptonChristoph BidlingmaierAlice CohenJohannes OldenburgSusan KearneyChristine KnollPhilip KuriakoseSuchitra AcharyaUlrike M ReissRoshni Daniel KulkarniMichelle L WitkopStefan LethagenSharyne DonfieldPetra LeBeauErik BerntorpJan AstermarkPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2020)
B-Natural provides data supporting an increased understanding of HB and its impact throughout life. The need for optimal disease control to normalize physical and psychosocial outcomes is underscored, and further analyses will contribute to an increased understanding of critical issues in HB.