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Factor VIII pharmacokinetics associates with genetic modifiers of VWF and FVIII clearance in an adult hemophilia A population.

Kenichi OgiwaraLaura L SwystunA Simonne PaineSylvia KepaSeon Jai ChoiJudit RejtöWilma HopmanIngrid PabingerDavid Lillicrap
Published in: Journal of thrombosis and haemostasis : JTH (2020)
VWF-FVIII binding activity and genetic determinants of VWF clearance are important contributors to FVIII pharmacokinetics in adult patients.
Keyphrases
  • genome wide
  • copy number
  • gene expression