How children and caregivers viewed the change from nusinersen to risdiplam for treating spinal muscular atrophy.
Caterina AgostoFrancesca BenedettiEleonora SalamonAnna MercanteSimonetta PapaLuca GiacomelliAnna SantiniFranca BeniniPublished in: Acta paediatrica (Oslo, Norway : 1992) (2022)
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