Impact of lumacaftor/ivacaftor on nutrition and growth in modulator-naïve children over 24 weeks.
Alyssa TindallRosara BassAsim MaqboolVirginia A Stallings
Published in: Journal of cystic fibrosis : official journal of the European Cystic Fibrosis Society (2024)
Overall, young children experienced favorable changes in nutritional and growth, with the exception of plasma ALA status in the first 24 weeks of lumacaftor/ivacaftor therapy.