Clinical efficacy of CFTR modulator therapy in people with cystic fibrosis carrying the I1234V mutation.
Bat El Bar AlumaJoel ReiterOri EfratiYael BezalelShlomit KelerMoshe AshkenaziAdi DaganYael BuchnikIdo SadrasMalena Cohen-CymberknohPublished in: Journal of cystic fibrosis : official journal of the European Cystic Fibrosis Society (2024)
This study supports a clinical benefit for CFTRm therapy in pwCF carrying the I1234V mutation.