Long-Term Efficacy and Safety of Eculizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria and High Disease Burden: Real-World Data From Korea.
Jin Seok KimJun Ho JangDeog-Yeon JoSeo-Yeon AhnSung Soo YoonJe Hwan LeeSung-Hyun KimChul Won ChoiHo Jin ShinMin-Kyoung KimJae Hoon LeeYeung Chul MunJee Hyun KongBokJin HyunHyunSun NamEunhye KimMin Joo KwakYong Kyun WonJong Wook LeePublished in: Journal of Korean medical science (2023)
These data provided evidence for the long-term efficacy and safety of eculizumab in Korean PNH patients with high disease burdens.