Teamwork makes the dream work: functional collaborations between families, scientists, and healthcare providers to drive progress in the treatment of Leigh Syndrome.
Jesse D MoreiraKaran K SmithSophia ZilberKasey WolebenJessica L FettermanPublished in: Orphanet journal of rare diseases (2023)
In this symposium review, we describe the research presented, the hurdles ahead, and strategies to better connect the Leigh syndrome community members to advance treatments for Leigh syndrome.