Time to Transplant in X-Linked Adrenoleukodystrophy.
Joshua Leith BonkowskyJacob WilkesPublished in: Journal of child neurology (2022)
We found that time to hematopoietic stem cell transplantation was >3 months for patients with cerebral adrenoleukodystrophy in the hospitals we evaluated. We noted differences in average time by race/ethnicity and by hospital. Our findings suggest opportunity to reduce time to transplant in cerebral adrenoleukodystrophy.