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NODAL variants are associated with a continuum of laterality defects from simple D-transposition of the great arteries to heterotaxy.

Zain DardasJawid M FatihAngad JollyMoez DawoodHaowei DuChristopher M GrochowskiEdward G JonesShalini N JhangianiXander H T WehrensPengfei LiuWeimin BiEric BoerwinkleJennifer E PoseyDonna M MuznyRichard A GibbsJames R. LupskiZeynep C AkdemirShaine Alaine Morris
Published in: Genome medicine (2024)
Our data further support a role for rare deleterious variants in NODAL as a cause for sporadic human laterality defects, expand the repertoire of observed anatomical complexity of potential cardiovascular anomalies, and implicate an allele specific gene dosage model.
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