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In Vivo Base Editing of Scn5a Rescues Type 3 Long QT Syndrome in Mice.

Man QiShuhong MaJingtong LiuXujie LiuJingjing WeiWen-Jing LuSiyao ZhangYun ChangYongshuai ZhangKejia ZhongYuting YanMin ZhuYabing SongYun-Dai ChenGuoliang HaoJianbing WangLi WangAndrew S LeeXiangbo ChenYongming WangFeng Lan
Published in: Circulation (2023)
allele, effectively ameliorating arrhythmia phenotypes. Our results offer a proof of concept for the treatment of hereditary arrhythmias.
Keyphrases
  • crispr cas
  • mouse model
  • high fat diet induced
  • congenital heart disease
  • metabolic syndrome
  • combination therapy
  • skeletal muscle
  • atrial fibrillation