In Vivo Base Editing of Scn5a Rescues Type 3 Long QT Syndrome in Mice.
Man QiShuhong MaJingtong LiuXujie LiuJingjing WeiWen-Jing LuSiyao ZhangYun ChangYongshuai ZhangKejia ZhongYuting YanMin ZhuYabing SongYun-Dai ChenGuoliang HaoJianbing WangLi WangAndrew S LeeXiangbo ChenYongming WangFeng LanPublished in: Circulation (2023)
allele, effectively ameliorating arrhythmia phenotypes. Our results offer a proof of concept for the treatment of hereditary arrhythmias.