Changing incentives to ACCELERATE drug development for paediatric cancer.
Teresa de RojasPamela KearnsPatricia BlancJeffrey SkolnikElizabeth FoxLeona KnoxRaphael RousseauFrançois DozNick BirdAndrew J PearsonGilles VassalPublished in: Cancer medicine (2023)
Additionally, to address the critical gap in the current framework where there is a complete lack of incentives to promote paediatric-specific cancer drug development, we propose the introduction of early rewards in the Orphan Regulation, with a variant on the US-Creating Hope Act and its priority review vouchers.