Fabry heterozygote mimicking multiple sclerosis.
Wai Yan YauMarzena J Fabis-PedriniAllan G KermodePublished in: BMJ case reports (2017)
Fabry's disease (FD) is a recognised mimic of multiple sclerosis (MS). It is an X-linked storage lysosomal disorder with deficiency of α-galactosidase A and enzyme replacement therapy is available. Patients with FD may satisfy modified McDonald criteria if the diagnosis of FD has not been pursued. We present a case of FD in a 65-year-old woman masquerading as benign MS for 40 years. She has recurrent posterior circulation stroke-like symptoms, hearing loss and acroparaesthesia, but typical radiological features of MS on MRI brain. Later she developed an ischaemic stroke, infiltrative cardiomyopathy and chronic renal failure. There was a missense mutation at p.R342Q in the galactodisdase alpha (GLA) gene. Neurologists need to consider FD and look for red flags in atypical MS cases and should not be over-reliant on MRI findings. Missed diagnosis of FD could lead to unnecessary immunosuppression, inappropriate disease counselling and missed treatment opportunity.
Keyphrases
- multiple sclerosis
- replacement therapy
- smoking cessation
- white matter
- mass spectrometry
- ms ms
- magnetic resonance imaging
- contrast enhanced
- heart failure
- atrial fibrillation
- genome wide
- copy number
- physical activity
- dna methylation
- human immunodeficiency virus
- gene expression
- computed tomography
- left ventricular
- resting state
- magnetic resonance
- autism spectrum disorder
- functional connectivity
- antiretroviral therapy