Natural history and long-term effects of variant protein reduction in non-V30M ATTR amyloidosis.
Taro YamashitaMitsuharu UedaToshiya NomuraTakahiro OkazakiMasamitsu OkadaYukimoto TsudaYasuteru InoueTeruaki MasudaYohei MisumiKotaro TakamatsuKonen ObayashiYukihiro InomataTaizo HibiYukio AndoPublished in: Neurology (2019)