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Spastic paraplegia type 46: novel and recurrent GBA2 gene variants in a compound heterozygous Italian patient with spastic ataxia phenotype.

Marta GattiStefania MagriDaniela Di BellaElisa SartoFranco TaroniCaterina MariottiLorenzo Nanetti
Published in: Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology (2021)
Clinical manifestations associated with GBA2 gene variants encompass a spectrum of overlapping phenotypes including cerebellar ataxia, spastic paraplegia, and Marinesco-Sjogren-like syndrome. We review previously reported cases of SPG46 and discuss possible genetic differential diagnosis.
Keyphrases
  • copy number
  • cerebral palsy
  • genome wide
  • botulinum toxin
  • early onset
  • upper limb
  • case report
  • dna methylation
  • genome wide identification