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Correction: Expert Group Consensus on early diagnosis and management of infantile-onset pompe disease in the Gulf Region.

Zuhair Al HassnanNadia Al HashmiNawal MakhseedTawfeg Ben OmranFatma Al JasmiAmal Al Teneiji
Published in: Orphanet journal of rare diseases (2023)
Keyphrases
  • late onset
  • clinical practice
  • replacement therapy
  • early onset