Multimodal and longitudinal evaluation of novel phenotype-genotype correlation of CLN3 isolated retinal degeneration in an hispanic female with heterozygous mutations c.944dup and c.1305C>G.
Lucas A Garza-GarzaPriscila Villarreal-MartinezRocio Villafuerte-de la CruzManuel Garza-LeónPublished in: Ophthalmic genetics (2023)
IRD severe phenotype associated with the variants c.944dup and c.1305C>G, which had previously only been associated with JCNL.