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A Trivalent Enzymatic System for Uricolytic Therapy of HPRT Deficiency and Lesch-Nyhan Disease.

Luca RondaMarialaura MarchettiRiccardo PianoAnastasia LiuzziRomina CorsiniRiccardo PercudaniStefano Bettati
Published in: Pharmaceutical research (2017)
Pharmaceutical restoration of the uricolytic pathway is a viable approach for the treatment of severe hyperuricemia.
Keyphrases
  • early onset
  • hydrogen peroxide
  • uric acid
  • stem cells
  • nitric oxide
  • combination therapy
  • mesenchymal stem cells