Real-world efficacy and safety of luspatercept and predictive factors of response in patients with transfusion-dependent β-thalassemia.
Daniele Lello PanzieriDario ConsonniNatalia ScaramelliniGuido AusendaFrancesca GranataNancy CaponioLorena DucaSimona LeoniSilvia ElliMarta FerraresiVittorio BolisCristina CurcioMilena Agata IrreraDiletta MairaGiovanna GraziadeiElena CassinerioMaria Domenica CappelliniRayan Bou-FakhredinValentina BrancaleoniIrene MottaPublished in: American journal of hematology (2024)