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Establishing Clinical Trial Endpoints in Selecting Patients for RPGR Retinal Gene Therapy.

Evita Evangelia ChristouAmandeep S JosanJasmina Cehajic-KapetanovicRobert E MacLaren
Published in: Translational vision science & technology (2024)
Biomarkers of visual function in RPGR-associated RP may lead to identification of appropriate patients for enrollment in clinical trials.
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