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Two novel bi-allelic KDELR2 missense variants cause osteogenesis imperfecta with neurodevelopmental features.

Stephanie EfthymiouIsabella HermanFatima RahmanNajwa AnwarReza MaroofianJanice YipTadahiro MitaniDaniel G CalameJill V HunterV Reid SuttonElif Yilmaz GulecRuizhi DuanJawid M FatihDana MarafiDavut PehlivanShalini N JhangianiRichard A GibbsJennifer E Poseynull nullShazia MaqboolJames R. LupskiHenry Houlden
Published in: American journal of medical genetics. Part A (2021)
Keyphrases
  • copy number
  • intellectual disability
  • bone regeneration