Login / Signup

Genetics, diagnosis, and future treatment strategies for primary ciliary dyskinesia.

M Leigh Anne DanielsPeadar G Noone
Published in: Expert opinion on orphan drugs (2014)
Although interest in clinical studies in non-CF bronchiectasis has increased in recent years, some of whom enroll patients with PCD, the literature regarding therapy for PCD as a distinct entity is lacking, as the numbers are small, and there have been no sub-analyses published. However, with improved screening and diagnostic methods, the development of clinical and research consortiums, and actively enrolling registries of PCD patients, the environment is conducive to perform longitudinal studies of disease course and therapeutic studies to alter that course.
Keyphrases