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Analysis of therapy monitoring in the International Congenital Adrenal Hyperplasia Registry.

Neil Richard LawrenceIrina BacilaJeremy DawsonJillian BryceSalma R AliErica L T van den AkkerTânia A S S BachegaFederico BaronioNiels H BirkebaekWalter BonfigHedi C van der GrintenEduardo C CostaLiat de VriesHeba ElsedfyAyla GüvenSabine Elisabeth HannemaVioleta IotovaHetty J van der KampMaría ClementeCorina R LichiardopolTatjana MilenkovicUta NeumannAnna NordenströmŞukran PoyrazoğluUrsina Probst-ScheideggerLuisa De SanctisRieko Tadokoro-CuccaroAjay ThankamonyAna VieitesZehra YavaşSyed Faisal AhmedNils P Krone
Published in: Clinical endocrinology (2022)
Registry data show large variability in 17OHP and D4 between centres. 17OHP correlates with D4 well when accounting for age. Prescribed HC dose per body surface area decreased with weight gain.
Keyphrases
  • weight gain
  • body mass index
  • birth weight
  • electronic health record
  • weight loss
  • big data
  • stem cells
  • machine learning
  • physical activity
  • cell therapy
  • data analysis
  • replacement therapy