Cyclosporine A in children with ABCA3 deficiency.

Xiaohua YangMaria E ForstnerIna RothenaignerMarina BulloTugba Sismanlar EyubogluAyse T AslanPhilipp LatzinKamyar HadianMatthias Griese

Published in: Pediatric pulmonology (2024)

CsA treatment might be helpful for certain patients with ABCA3 deficiency, however, currently strong clinical supporting evidence is lacking. Appropriate trials are necessary to overcome this unmet need.

Keyphrases

replacement therapy
young adults
smoking cessation