Frataxin deficiency alters gene expression in Friedreich ataxia derived IPSC-neurons and cardiomyocytes.
Mariana B AnguloAlexander BertalovitzMariana A ArgenzianoJiajia YangAarti PatelTheresa ZesiewiczThomas V McDonaldPublished in: Molecular genetics & genomic medicine (2022)
These results offer novel insight into specific roles of frataxin deficiency pathogenesis in neurons and cardiomyocytes.