Measurement Properties of 2 Novel PROs, the Pompe Disease Symptom Scale and Pompe Disease Impact Scale, in the COMET Study.
Mazen M DimachkiePriya S KishnaniCristina IvanescuGiulio FloreChad GwaltneyNadine A M E van der BeekAlaa HamedKristina An HaackLaurence PollissardEileen BaranowskiSusan E SparksPronabesh DasMahapatranull nullPublished in: Neurology. Clinical practice (2023)
ClinicalTrials.gov identifier: NCT02782741.