A 10-year follow-up of high-dose ambroxol treatment combined with enzyme replacement therapy for neuropathic Gaucher disease.
Soojin HwangHyunwoo BaeJi-Hee YoonDohyung KimHyo-Sang DoSun Hee HeoSoyoung KimHan Wook YooMajdolen IstaitiAri ZimranBeom-Hee LeePublished in: American journal of hematology (2024)
High-dose ambroxol therapy combined with ERT in patients with neuropathic Gaucher disease.