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Pre-ataxic Changes of Clinical Scales and Eye Movement in Machado-Joseph Disease: BIGPRO Study.

Camila Maria de OliveiraVanessa Bielefeldt LeottiGabriela BolzanAmanda Henz CappelliAnastacia Guimarães RochaGabriela EccoNathalia KerstingMariana RieckAna Carolina MartinsLucas Schenatto SenaMaria-Luiza Saraiva-PereiraLaura Bannach Jardim
Published in: Movement disorders : official journal of the Movement Disorder Society (2021)
Clinical scales and video-oculography variables were already altered in pre-ataxic SCA3/MJD carriers and worsened with time. NESSCA, ICARS, INAScount, VORr, main sequence of vertical volitional saccades, and SPV-GE are good candidates to measure preclinical changes in SCA3/MJD. © 2021 International Parkinson and Movement Disorder Society.
Keyphrases
  • stem cells
  • cell therapy
  • mesenchymal stem cells