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A Novel Smad7 Genetic Variant Mapping on the Genomic Region Targeted by Mongersen Is Associated with Crohn's Disease.

Davide Di FuscoIrene MarafiniCarmine StolfiEdoardo TronconeSara OnaliElisabetta LolliFlavio CaprioliStefano MazzaCascella RaffaellaLaura ManzoPaola BorgianiPaolo GiuffridaAntonio Di SabatinoIvan MonteleoneGiovanni Monteleone
Published in: Biomedicines (2020)
This is the first study to show an association between Smad7 rs144204026 SNP and CD patients. Data indicate that such a variant does not negatively influence the in vitro inhibitory effect of Smad7 AS on Smad7.
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