Afamelanotide for Treatment of the Protoporphyrias: Impact on Quality of Life and Laboratory Parameters in a US Cohort.

Rebecca K LeafHetanshi NaikPaul Y JiangSarina B ElmariahPamela HodgesJennifer MeadJohn TrinidadBehnam SaberiBenny TranSarah ValianteFrancesca MernickDavid E LeafKarl E Anderson Amy K Dickey

Published in: Life (Basel, Switzerland) (2024)

This study highlights a dramatic clinical benefit of afamelanotide in relation to light tolerance and QoL in protoporphyria, albeit without improvement in protoporphyrin levels or measures of liver function.

Keyphrases

replacement therapy
smoking cessation