Haploidentical hematopoietic stem cell transplantation with busulfan, cyclophosphamide, and fludarabine conditioning for X-linked adrenal cerebral leukodystrophy.
Yao ChenLan-Ping XuXiao-Hui ZhangHuan ChenKai-Yan LiuJiong QingYan-Ling YangXiao-Jun HuangPublished in: Pediatric transplantation (2024)
BFC regimen used in haploidentical SCT was administered safely without major transplant-related complications even in symptomatic patients, and neurological symptoms were stabilized after SCT.