Diagnostic value of plasma lysosphingolipids levels in a Niemann-Pick disease type C patient with transient neonatal cholestasis.
Fatma Derya BulutNeslihan Ekşi BozbulutÖzge ÖzalpBuket DalgiçNeslihan Önenli MunganHabibe Koç UçarGürsel BiberoğluPublished in: Journal of pediatric endocrinology & metabolism : JPEM (2022)
gene, lysosomal biomarkers play an important role when genetic analyses are inconclusive.