Login / Signup

Istore: a project on innovative statistical methodologies to improve rare diseases clinical trials in limited populations.

Stefanie SchoenenJohan VerbeeckLukas KoletzkoIsabella BrambillaMathieu KuchenbuchMaya DiraniGeorg ZimmermannHolger DetteRalf-Dieter HilgersGeert MolenberghsRima Nabbout
Published in: Orphanet journal of rare diseases (2024)
Through its expected results, iSTORE will contribute to the rare diseases research field by providing an approach to better inform about and thus being able to plan a clinical trial. The methodological derivations can be synchronized and transferability will be outlined.
Keyphrases
  • clinical trial
  • phase ii
  • open label
  • quality improvement
  • study protocol
  • double blind
  • phase iii