Molecular phenotypes segregate missense mutations in SLC13A5 Epilepsy.
Valeria Jaramillo-MartinezSouad R SennouneElena B TikhonovaAndrey L KaramyshevVadivel GanapathyIna L UrbatschPublished in: bioRxiv : the preprint server for biology (2024)
Loss-of-function mutations in the SLC13A5 causes SLC13A5-Epilepsy, a devastating disease characterized by neonatal epilepsy. Currently no cure is available. We clarify the molecular-level defects to guide future developments for phenotype-specific treatment of disease-causing mutations.
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