Psychometric evaluation of the NTDT-PRO questionnaire for assessing symptoms in patients with non-transfusion-dependent beta-thalassaemia.
Ali T TaherKhaled M MusallamVip ViprakasitAntonis KattamisJennifer Lord-BessenAylin YucelShien GuoChristopher G PelligraAlan L ShieldsJeevan K ShettyDimana MitevaLuciana Moro BuenoMaria Domenica CappelliniPublished in: BMJ open (2023)
The NTDT-PRO demonstrated adequate psychometric properties to assess anaemia-related symptoms in adults with NTDT and can be used to evaluate treatment efficacy in clinical trials.