Psychometric validation of the Pyruvate Kinase Deficiency Diary and Pyruvate Kinase Deficiency Impact Assessment in adults in the phase 3 ACTIVATE trial.
David A AndraeRachael F GraceAdrian JewettBrandon FosterRobert J KlaassenSam SalekJunlong LiFeng TaiAudra N BoscoeErin ZagadailovPublished in: Journal of patient-reported outcomes (2023)
gov/ct2/show/NCT03548220 .