Identifying responders to elamipretide in Barth syndrome: Hierarchical clustering for time series data.
Jef Van den EyndeBhargava ChinniHilary VernonW Reid ThompsonBrittany HornbyShelby KuttyCedric ManlhiotPublished in: Orphanet journal of rare diseases (2023)
In this proof-of-concept study, we demonstrated that continuously acquired physiological measurements from wearable devices can be used to predict functional status and response to treatment among patients with BTHS.