Effects of PK-guided prophylaxis on clinical outcomes and FVIII consumption for patients with moderate to severe Haemophilia A.

Guy Aaron YoungMichael U CallaghanVinod BalasaAmit SoniSanjay AhujaJonathan C RobertsMindy L SimpsonHande Kızılocak Andrew FrickAli G MokdadShan XingJorge Caicedo

Published in: Haemophilia : the official journal of the World Federation of Hemophilia (2023)

PK-guided prophylaxis has the potential to improve clinical outcomes without increase in cost of therapy for patients maintaining product and can aid in maintaining effective protection against bleeds in those switching product.

Keyphrases

end stage renal disease
ejection fraction
newly diagnosed
peritoneal dialysis
prognostic factors
high intensity
patient reported