Allogeneic hematopoietic stem cell transplantation in patients with childhood cerebral adrenoleukodystrophy: A single-center experience "Better prognosis in earlier stage".
Koray YalÇinSuna S ÇelenHayriye DalogluMustafa Kemal DemirSeda ÖztürkmenDayanat PasayevSuleimen ZhumatayevVedat UygunVolkan HazarGulsun KarasuMehmet Akif YesilipekPublished in: Pediatric transplantation (2021)
This study demonstrated that early HSCT is vital in patients with cALD. The early-stage disease had a significant survival advantage and free from disease progression after HSCT.