Functional independence of Taiwanese patients with mucopolysaccharidoses.
Chung-Lin LeeHsiang-Yu LinChih-Kuang ChuangHuei-Ching ChiuRu-Yi TuYou-Hsin HuangWuh-Liang HwuFuu-Jen TsaiPao-Chin ChiuDau-Ming NiuYann-Jang ChenMei-Chyn ChaoTung-Ming ChangJu-Li LinChia-Ying ChangYu-Chia KaoShuan-Pei LinPublished in: Molecular genetics & genomic medicine (2019)
MPS patients require support and supervision in self-care tasks. For cognition tasks, MPS IIIB patients also require help. This questionnaire is useful to identify the strengths and limitations of MPS patients.