The effects of transitioning from immediate release to extended release cysteamine therapy in Norwegian patients with nephropathic cystinosis: a retrospective study.
Anna BjerreSonja Amdal AaseMaria RadtkeChristian SivaHelga GudmundsdottirBrita ForsbergBerit WoldsethDamien BrackmanPublished in: Pediatric nephrology (Berlin, Germany) (2023)
The results from this long-term retrospective study indicate that switching from IR- to ER-cysteamine was feasible and well tolerated under routine clinical practice. ER-cysteamine allowed satisfactory disease control over the long period considered. A higher resolution version of the Graphical abstract is available as Supplementary information.