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Impaired diaphragmatic motility in treatment-naive adult patients with spinal muscular atrophy improved during nusinersen treatment.

Maren FreigangSimona LangnerAndreas HermannRené Günther
Published in: Muscle & nerve (2023)
Diaphragm ultrasound imaging can provide disease- and treatment-relevant information that is not identified during routine clinical assessments and may therefore be a valuable complementary outcome measure.
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