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A post hoc analysis of PROTECT VIII kids assessing long-term efficacy and safety of damoctocog alfa pegol in adolescents with severe haemophilia A.

Sanjay AhujaTina T BissMonika Maas EnriquezMaria Elisa MancusoMacGregor SteeleGili Kenet
Published in: European journal of haematology (2024)
Damoctocog alfa pegol is efficacious with a favourable safety profile in adolescents with haemophilia A, supporting its long-term use in children and adolescents.
Keyphrases
  • young adults
  • physical activity
  • replacement therapy
  • early onset
  • smoking cessation