Hematopoietic Stem Cell Transplantation in Late-Onset Krabbe Disease: No Evidence of Worsening Demyelination and Axonal Loss 4 Years Post-allograft.

Cornelia LauleIrene M VavasourElham ShahinfardBurkhard MädlerJing ZhangDavid K B LiAlex L MacKaySandra M Sirrs

Published in: Journal of neuroimaging : official journal of the American Society of Neuroimaging (2018)

Clinical evidence and stability of advanced MR measures related to myelin and axons supports HSCT as an effective treatment strategy for stopping progression associated with late-onset Krabbe disease.

Keyphrases

late onset
early onset
spinal cord injury
acute myeloid leukemia
magnetic resonance
multiple sclerosis
magnetic resonance imaging
optical coherence tomography
replacement therapy
drug induced
smoking cessation