Validation of the parent-proxy version of the pediatric Charcot-Marie-Tooth disease quality of life instrument for children aged 0-7 years.
Tong Tong WuRichard S FinkelCarly E SiskindShawna M E FeelyJoshua BurnsMary M ReillyFrancesco MuntoniEvelin MilevTimothy EstilowMichael E ShySindhu Ramchandrennull nullPublished in: Journal of the peripheral nervous system : JPNS (2023)
The parent-proxy version of the pCMT-QOL outcome measure, known as the pCMT-QOL (0-7 years parent-proxy) is a valid and sensitive proxy measure of health-related QOL for children aged 0-7 years with CMT.